All articles tagged with #hereditary angioedema
Originally Published 2 months ago — by Investor's Business Daily
Crispr and Intellia stocks surged following promising updates on their gene-editing therapies, with Crispr showing potential for a one-time cholesterol treatment and Intellia demonstrating a near-cure for hereditary angioedema, leading to significant stock gains despite recent setbacks in the sector.
Originally Published 1 year ago — by Good News Network
A single-dose gene therapy using CRISPR has shown promising results in treating hereditary angioedema, a rare genetic disorder causing painful and potentially fatal swelling. Patients in a human trial reported dramatic improvements in their health and quality of life, with some describing it as a "medical magic wand." The treatment corrects the C1 kallikrein gene and has the potential to transform the lives of those affected by the condition, although it comes with a high cost.
Originally Published 1 year ago — by The Guardian
A groundbreaking gene therapy has shown promising results in treating hereditary angioedema, a rare disorder causing painful and potentially fatal swelling. Patients in the trial experienced dramatic improvements, with some being able to come off long-term medication and return to normal life. The therapy, using Crispr gene editing, aims to provide a permanent cure by targeting the genetic mutation causing the condition. While larger trials are ongoing, the high cost of one-shot gene therapies may limit accessibility, but the results offer hope for a potential cure for some sufferers.
Originally Published 2 years ago — by Good News Network
The FDA has approved Intellia Therapeutics to begin testing a drug that uses CRISPR gene editing in vivo, marking the first time ever that the FDA has approved such testing. The drug would prevent swelling attacks in people with a genetic condition called hereditary angioedema. Typically, treatments and drugs that utilize CRISPR take place outside the body, but Intellia's edited media finds its own way to the liver rather than being injected there.