Gene Therapy Revolutionizes Teen's Life
Originally Published 4 months ago — by The Times
A groundbreaking gene therapy developed by UCL and GOSH has transformed the life of 19-year-old Remi Pereszczak, who suffered from a rare genetic condition called CGD. The therapy, which involves reprogramming his own stem cells, has enabled him to live a healthier, more normal life and attend university. GOSH's new capacity to produce personalized gene therapies in-house promises to accelerate treatment for rare diseases and has broader implications for medicine, including potential cancer cures.