All articles tagged with #cerebral folate deficiency
Families have been using leucovorin, a drug originally for cancer, to treat autism symptoms, gaining attention after President Trump mentioned it. While some studies suggest potential benefits, the evidence is limited and the FDA's recent move to update the drug's label is considered unusual and controversial due to weak supporting data. Experts emphasize the need for more research and caution in its use.
Leucovorin, a drug approved for chemotherapy side effects, is being explored as a potential treatment for autism related to cerebral folate deficiency. While some small studies and anecdotal reports suggest improvements in communication and behavior, there is not enough rigorous scientific evidence to confirm its safety and efficacy for autism, raising concerns about premature approval and unregulated use. The FDA plans to update its labeling to reflect potential benefits, but experts warn against overestimating the current evidence.
The FDA approved leucovorin, a form of folic acid, which was suggested by President Trump as a potential treatment for autism symptoms, based on data indicating it may improve symptoms related to cerebral folate deficiency, a condition associated with neuropsychiatric symptoms including autistic features.