FDA Panel Raises Concerns Over Sarepta's Gene Therapy for Duchenne Muscular Dystrophy
TL;DR Summary
The FDA is holding an advisory panel meeting to review clinical data on Sarepta Therapeutics' experimental gene therapy for Duchenne muscular dystrophy. Many Duchenne patients and their families view the therapy as the best hope for slowing the fatal muscle-wasting disease. The meeting is expected to be contentious and could have a significant impact on the future of the therapy.
Topics:business#advisory-panel#duchenne-muscular-dystrophy#fda#gene-therapy#healthcare#sarepta-therapeutics
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