"Record-breaking $4.25 Million Gene Therapy Raises Access Concerns"
A new therapy for a rare genetic disease has become the world's most expensive drug, priced at $4.25 million. The treatment targets a rare genetic disorder that causes children to rapidly age and usually results in death during the teenage years. The high cost of the therapy has sparked concerns about accessibility and affordability, raising questions about the pricing of life-saving treatments for rare diseases.