Stealth BioResubmits Rare Disease Drug Application Amid FDA Challenges
TL;DR Summary
Stealth BioTherapeutics disclosed an FDA rejection letter to rally support for its experimental drug for Barth syndrome, a rare disease affecting about 150 people in the U.S., amid ongoing struggles to meet regulatory requirements and concerns over the company's future.
Topics:business#barth-syndrome#fda-rejection#healthcare#rare-disease#regulatory-approval#stealth-biotherapeutics
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